This paper is in the following e-collection/theme issue:

RCTs - Protocols/Proposals (funded, already peer-reviewed, non-eHealth) (172) Cardiac Disease Management (94) Pharmacology and Pharmaceutics (66) Drug Repurposing and Off-Label Use (25) Chronic Conditions (270)

Published on in Vol 10, No 5 (2021): May

Preprints (earlier versions) of this paper are available at https://preprints.jmir.org/preprint/22533, first published .
Treatment of Barth Syndrome by Cardiolipin Manipulation (CARDIOMAN) With Bezafibrate: Protocol for a Randomized Placebo-Controlled Pilot Trial Conducted in the Nationally Commissioned Barth Syndrome Service

Treatment of Barth Syndrome by Cardiolipin Manipulation (CARDIOMAN) With Bezafibrate: Protocol for a Randomized Placebo-Controlled Pilot Trial Conducted in the Nationally Commissioned Barth Syndrome Service

Treatment of Barth Syndrome by Cardiolipin Manipulation (CARDIOMAN) With Bezafibrate: Protocol for a Randomized Placebo-Controlled Pilot Trial Conducted in the Nationally Commissioned Barth Syndrome Service

Authors of this article:

Lucy Dabner1 Author Orcid Image ;   Guido E Pieles2, 3 Author Orcid Image ;   Colin G Steward4 Author Orcid Image ;   Julian P Hamilton-Shield5 Author Orcid Image ;   Andrew R Ness5, 6 Author Orcid Image ;   Chris A Rogers1 Author Orcid Image ;   Chiara Bucciarelli-Ducci3, 7 Author Orcid Image ;   Rosemary Greenwood8 Author Orcid Image ;   Lucy Ellis1 Author Orcid Image ;   Karen Sheehan9 Author Orcid Image ;   Barnaby C Reeves1 Author Orcid Image
Article Authors Cited by (13) Tweetations (4) Metrics

Lucy Dabner   1 , MSc ;   Guido E Pieles   2, 3 , MScHE, DPhil, PhD, MD ;   Colin G Steward   4 , MD ;   Julian P Hamilton-Shield   5 , MD ;   Andrew R Ness   5, 6 , PhD ;   Chris A Rogers   1 , PhD ;   Chiara Bucciarelli-Ducci   3, 7 , PhD, MD ;   Rosemary Greenwood   8 , MSc ;   Lucy Ellis   1 , MSc ;   Karen Sheehan   9 , MSc ;   Barnaby C Reeves   1 , DPhil

1 Bristol Trials Centre (Clinical Trials and Evaluation Unit), Bristol Medical School, University of Bristol, Bristol, United Kingdom

2 Bristol Congenital Heart Centre, University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom

3 National Institute of Health Research (NIHR) Biomedical Research Centre (Cardiovascular theme), University Hospitals Bristol and Weston NHS Foundation Trust and University of Bristol, Bristol, United Kingdom

4 School of Cellular and Molecular Medicine, University of Bristol, Bristol, United Kingdom

5 NIHR Biomedical Research Centre (Nutrition theme), University Hospitals Bristol and Weston NHS Foundation Trust and University of Bristol, Bristol, United Kingdom

6 Bristol Dental School, University of Bristol, Bristol, United Kingdom

7 Bristol Heart Institute, University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom

8 Research Design Service South West, National Institute for Health Research, Bristol, United Kingdom

9 University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom

Corresponding Author:

  • Lucy Dabner, MSc
  • Bristol Trials Centre (Clinical Trials and Evaluation Unit)
  • Bristol Medical School
  • University of Bristol
  • Upper Maudlin St
  • Level 7, Bristol Royal Infirmary
  • Bristol, BS2 8HW
  • United Kingdom
  • Phone: 44 (0)1173422374
  • Email: lucy.dabner@bristol.ac.uk