Published on in Vol 12 (2023)

Preprints (earlier versions) of this paper are available at https://preprints.jmir.org/preprint/42032, first published .
An Exploratory Trial of EPI-589 in Amyotrophic Lateral Sclerosis (EPIC-ALS): Protocol for a Multicenter, Open-Labeled, 24-Week, Single-Group Study

An Exploratory Trial of EPI-589 in Amyotrophic Lateral Sclerosis (EPIC-ALS): Protocol for a Multicenter, Open-Labeled, 24-Week, Single-Group Study

An Exploratory Trial of EPI-589 in Amyotrophic Lateral Sclerosis (EPIC-ALS): Protocol for a Multicenter, Open-Labeled, 24-Week, Single-Group Study

Shotaro Haji   1 , MD ;   Koji Fujita   1 , MD ;   Ryosuke Oki   1 , MD ;   Yusuke Osaki   1 , MD ;   Ryosuke Miyamoto   1 , MD ;   Hiroyuki Morino   2 , MD ;   Seiichi Nagano   3, 4 , MD ;   Naoki Atsuta   5 , MD ;   Yuki Kanazawa   6 , PhD ;   Yuki Matsumoto   7 , PhD ;   Atsuko Arisawa   8 , MD ;   Hisashi Kawai   9 , MD ;   Yasutaka Sato   10 , BSc ;   Satoshi Sakaguchi   10 , MD ;   Kenta Yagi   10 , PhD ;   Tatsuto Hamatani   11 , PhD ;   Tatsuo Kagimura   12 , PhD ;   Hiroaki Yanagawa   10 , MD ;   Hideki Mochizuki   3 , MD ;   Manabu Doyu   5 , MD ;   Gen Sobue   13 , MD ;   Masafumi Harada   7 , MD ;   Yuishin Izumi   1 , MD

1 Department of Neurology, Tokushima University Graduate School of Biomedical Sciences, Tokushima, JP

2 Department of Medical Genetics, Tokushima University Graduate School of Biomedical Sciences, Tokushima, JP

3 Department of Neurology, Osaka University Graduate School of Medicine, Suita, JP

4 Department of Neurotherapeutics, Osaka University Graduate School of Medicine, Suita, JP

5 Department of Neurology, Aichi Medical University School of Medicine, Nagakute, JP

6 Department of Biomedical Information Sciences, Tokushima University Graduate School of Biomedical Sciences, Tokushima, JP

7 Department of Radiology, Tokushima University Graduate School of Biomedical Sciences, Tokushima, JP

8 Department of Diagnostic and Interventional Radiology, Osaka University Graduate School of Medicine, Suita, JP

9 Department of Radiology, Aichi Medical University School of Medicine, Nagakute, JP

10 Clinical Research Center for Developmental Therapeutics, Tokushima University Hospital, Tokushima, JP

11 Sumitomo Pharma Co, Ltd, Osaka, JP

12 The Translational Research Center for Medical Innovation, Foundation for Biomedical Research and Innovation at Kobe, Kobe, JP

13 Aichi Medical University School of Medicine, Nagakute, JP

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